With LUXTURNA,

Imagine where you can go

LUXTURNA is the first FDA-approved gene therapy for a genetic disease

Photographs are not of actual patients.

LUXTURNA is a one-time gene therapy for individuals with an inherited retinal disease due to mutations in both copies of the RPE65 gene. Individuals must also have enough remaining cells in the retina.

About LUXTURNA

Get more information on how this gene therapy works

Discover LUXTURNA
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Take Your First Step

Learn the steps for determining if LUXTURNA may be right for you

Get Started
Take the Simple Screener

Find out if you are a possible candidate for an RPE65 genetic test, which can only be ordered by your healthcare professional

Find a Specialist

Locate a specialist who can help with genetic testing and provide more information on Inherited Retinal Diseases

Sign Up

Stay up to date on information about LUXTURNA

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Patient Support

Get to know Spark Therapeutics Generation Patient ServicesSM, our support program for eligible* patients

Find out more

*Participation in Spark Therapeutics Generation Patient ServicesSM is voluntary. You may choose to participate in all, some, or none of the services offered. Participating or deciding not to participate in these services will have no effect on your ability to get treatment or the nature of your treatment or care. Generation Patient Services does not provide medical advice. You should always rely on the direction of your healthcare professional for treatment and care.

*Participation in Spark Therapeutics Generation Patient ServicesSM is voluntary. You may choose to participate in all, some, or none of the services offered. Participating or deciding not to participate in these services will have no effect on your ability to get treatment or the nature of your treatment or care. Generation Patient Services does not provide medical advice. You should always rely on the direction of your healthcare professional for treatment and care.